Pipeline
Expanding our pipeline through Italfarmaco's internal R&D + external innovation
As the U.S. rare disease affiliate of the family-owned global pharmaceutical company Italfarmaco, we are positioned to support the commercialization of products in Italfarmaco’s pipeline here in the United States. We are also actively seeking partners with high-quality assets backed by strong data so we can bring our focus, agility, speed and expertise to deliver real value for people living with rare diseases in need of treatment options.
Disease Area
Neuromuscular Disorder
Givinostat
Duchenne muscular dystrophy
Givinostat
Becker muscular dystrophy
Disease Area
Hematological Disease
Givinostat
Polycythemia Vera
Clinical Studies
We remain focused on generating additional data to support the safe and effective use of therapies.